
Nature is investigating concerns surrounding a paper at the heart of a news story published last week on the death of a 6-year-old girl following a gene therapy treatment in China.
The paper, published in February by a team led by neuroscientist Zilong Qiu of Shanghai Jiao Tong University School of Medicine in China, described preclinical work for a gene-editing treatment for Snijders Blok-Campeau syndrome, a neurodevelopmental disorder.
As we reported in collaboration with Science, the work was funded in part by the family of a 6-year-old girl with the condition. The family had approached Qiu based on work he had done with gene therapy for Rett syndrome, a disorder that also causes developmental delay. The parents ended up paying $860,000 to fund preclinical work for a gene-editing treatment for their daughter, who died of a severe immune reaction to the therapy seven days after receiving it.
Continue reading Journal, university investigations launched into gene-editing death following Science-Retraction Watch reporting







